On Wednesday 28 February 2024, F. Catalano will defend the doctoral thesis titled: ‘Lentiviral Gene Therapy for Hunter Syndrome and Pompe Disease: Next Generation Therapies‘.
- Promotor
- Promotor
- Date
- Wednesday 28 Feb 2024, 13:00 - 14:30
- Type
- PhD defence
- Space
- Professor Andries Querido room
- Building
- Education Center
- Location
- Erasmus MC
Brief summary on the aim of the doctoral thesis:
Over the past several decades, Hematopoietic Stem and Progenitor Cell-mediated Lentiviral Gene Therapy (HSPC-LVGT) has been explored as a treatment for various inherited disorders, including metabolic diseases. The enduring clinical benefits reported in numerous trials have encouraged our laboratory to commence the Pompe and Hunter gene therapy projects, where we aimed to examine the therapeutic potential of HSPC-LVGT for the treatment of these two diseases. This thesis encloses the resulting preclinical findings, representing the foundation for future clinical applications of this approach.
- More information
The public defence will begin exactly at 13.00 hrs. The doors will be closed once the public defence starts, latecomers can access the hall via the fourth floor. Due to the solemn nature of the ceremony, we recommend that you do not take children under the age of 6 to the first part of the ceremony.
